Gene Therapy Working Group
The EAHAD Gene Therapy Working Group was formed in 2019. The working group will strive to be at the forefront of providing critical information to physicians and patients about gene therapy in terms of practicability and safety.
Its goals are:
- To investigate gene therapy safety and its outcome parameters.
- To provide updates on recent developments in terms of alanine aminotransferase (ALT) results and safety outcomes.
- To collect data on the different gene therapy trials, tests, and adverse events.
- To inform patients and medical professionals.
Members
2025 Webinars
EAHAD Gene Therapy Trials Database
The EAHAD-GTD is a user-friendly, publicly accessible database gathering the latest gene therapy results focusing on safety issues, reporting only the published cases. It is designed to serve physicians and researchers actively involved in gene therapy research and clinical practice to connect them with the latest insights into ongoing and completed clinical trials, offering a comprehensive understanding of recent advancements in gene therapy for haemophilia.